Rare Diseases and Orphan Drugs: A Life-Saving Partnership

Rare Diseases and Orphan Drugs: A Life-Saving Partnership

Three decades ago, rare disease patients caused a “ruckus” and demanded Congress take action to pass the Orphan Drug Act.

Paul Melmeyer with the National Organization for Rare Disorders explains that the Orphan Drug Act has played a critical role in the development of hundreds of treatments and orphan drugs for rare diseases.

Find out more about how the Orphan Drug Act is helping patients.

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